Pediatric Kidney Disease Research & Clinical Trials
Clinical trials are studies to develop, produce and evaluate the effectiveness of new treatments and therapies for diseases.
Jerome C. Lane, MD, has major areas of clinical interest including pathogenesis of hemolytic-uremic syndrome (HUS), and mechanisms of clinical progression in congenital renal disease and urogenital malformations. In addition, Dr. Lane has a considerable background and laboratory experience in renal transport of major ions.
This is a long-term, open-label study of the safety, tolerability and effectiveness of RP103 in cystinosis patients who are naïve to any form of cysteamine treatment. Subjects will receive RP103 treat...