Publications

Combination molecular therapies for type 1 spinal muscular atrophy

Harada, Y.; Rao, V. K.; Arya, K.; Kuntz, N. L.; DiDonato, C. J.; Napchan-Pomerantz, G.; Agarwal, A.; Stefans, V.; Katsuno, M.; Veerapandiyan, A. Muscle Nerve. 2020 Jul 28

Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial

Clemens, P. R.; Rao, V. K.; Connolly, A. M.; Harper, A. D.; Mah, J. K.; Smith, E. C.; McDonald, C. M.; Zaidman, C. M.; Morgenroth, L. P.; Osaki, H.; Satou, Y.; Yamashita, T.; Hoffman, E. P. JAMA Neurol. 2020 May 27

The care of patients with Duchenne, Becker, and other muscular dystrophies in the COVID-19 pandemic

Veerapandiyan, A.; Wagner, K. R.; Apkon, S.; McDonald, C. M.; Mathews, K. D.; Parsons, J. A.; Wong, B. L.; Eichinger, K.; Shieh, P. B.; Butterfield, R. J.; Rao, V. K.; Smith, E. C.; Proud, C. M.; Connolly, A. M.; Ciafaloni, E. Muscle Nerve. 2020 Apr 25; 62(1):41-45

Spinal muscular atrophy care in the COVID-19 pandemic era

Veerapandiyan, A.; Connolly, A. M.; Finkel, R. S.; Arya, K.; Mathews, K. D.; Smith, E. C.; Castro, D.; Butterfield, R. J.; Parsons, J. A.; Servais, L.; Kuntz, N.; Rao, V. K.; Brandsema, J. F.; Mercuri, E.; Ciafaloni, E. Muscle Nerve. 2020 Apr 25; 62(1):46-49

Utility of Repetitive Nerve Stimulation in Myopathies

Schwaede, A.; Buehner, A. N.; Rao, V. K. Pediatr Neurol Briefs. 2020 Mar 17; 34:4